An ultimate mouse model of gene therapy for Alpha1 Anti-trypsin deficiency

Project specs

Format

2D

Contact

Marina Zieger

Country

USA

Length

1:30

Summary

This animation, produced in conjunction with Dr. Mueller and his team at the University of Massachusetts Medical School, looks at how an ‘Ultimate Mouse Model’ is being used to develop gene therapy for Alpha1 Anti-trypsin deficiency.

Researcher Profile

Dual-function AAV vector to prevent alpha-1 antitrypsin deficiency

The Mueller lab at UMass Medical School has developed a…