Dual-function AAV vector to prevent alpha-1 antitrypsin deficiency

Project specs

Contact

Gwladys Gernoux 1

Country

USA

Length

1:30

Summary

The Mueller lab at UMass Medical School has developed a dual function approach using AAV vectors targeting both lung and liver diseases in alpha-1 antitrypsin deficient (AATD) patients. This animation is an overview of this research.

Researcher Profile

How drugs and nutrients get into cells

A 3-minute introduction into the groundbreaking work into the synthetic…