A new treatment for ALS
Summary
A new therapy approach for C9ORF72 linked ALS: using AAV9 as a vehicle to deliver an artificial microRNA to target aberrant transcripts. A single dose will permanently treat motor neurons and prevent cell death.
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Summary
A new therapy approach for C9ORF72 linked ALS: using AAV9 as a vehicle to deliver an artificial microRNA to target aberrant transcripts. A single dose will permanently treat motor neurons and prevent cell death.
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